Translating the genomics revolution: The need for an international gene therapy consortium for monogenic diseases

Jacques P. Tremblay, Xiao Xiao, Annemieke Aartsma-Rus, Carlos Barbas, Helen M. Blau, Adam J. Bogdanove, Kym Boycott, Serge Braun, Xandra O. Breakefield, Juan A. Bueren, Michael Buschmann, Barry J. Byrne, Michele Calos, Toni Cathomen, Jeffrey Chamberlain, Marinee Chuah, Kenneth Cornetta, Kay E. Davies, J. George Dickson, Philippe DuchateauTerence R. Flotte, Daniel Gaudet, Charles A. Gersbach, Renald Gilbert, Joseph Glorioso, Roland W. Herzog, Katherine A. High, Wenlin Huang, Johnny Huard, J. Keith Joung, Depei Liu, Dexi Liu, Hanns Lochmüller, Lawrence Lustig, Jeffrey Martens, Bernard Massie, Fulvio Mavilio, Jerry R. Mendell, Amit Nathwani, Katherine Ponder, Matthew Porteus, Jack Puymirat, Jude Samulski, Shin'Ichi Takeda, Adrian Thrasher, Thierry Vandendriessche, Yuquan Wei, James M. Wilson, Steve D. Wilton, John H. Wolfe, Guangping Gao

Research output: Contribution to journalLetter

10 Citations (Scopus)
Original languageEnglish (US)
Pages (from-to)266-268
Number of pages3
JournalMolecular Therapy
Volume21
Issue number2
DOIs
StatePublished - Feb 1 2013

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International Cooperation
Genomics
Genetic Therapy
Biomedical Research

ASJC Scopus subject areas

  • Molecular Medicine
  • Molecular Biology
  • Genetics
  • Pharmacology
  • Drug Discovery

Cite this

Tremblay, J. P., Xiao, X., Aartsma-Rus, A., Barbas, C., Blau, H. M., Bogdanove, A. J., ... Gao, G. (2013). Translating the genomics revolution: The need for an international gene therapy consortium for monogenic diseases. Molecular Therapy, 21(2), 266-268. https://doi.org/10.1038/mt.2013.4

Translating the genomics revolution : The need for an international gene therapy consortium for monogenic diseases. / Tremblay, Jacques P.; Xiao, Xiao; Aartsma-Rus, Annemieke; Barbas, Carlos; Blau, Helen M.; Bogdanove, Adam J.; Boycott, Kym; Braun, Serge; Breakefield, Xandra O.; Bueren, Juan A.; Buschmann, Michael; Byrne, Barry J.; Calos, Michele; Cathomen, Toni; Chamberlain, Jeffrey; Chuah, Marinee; Cornetta, Kenneth; Davies, Kay E.; Dickson, J. George; Duchateau, Philippe; Flotte, Terence R.; Gaudet, Daniel; Gersbach, Charles A.; Gilbert, Renald; Glorioso, Joseph; Herzog, Roland W.; High, Katherine A.; Huang, Wenlin; Huard, Johnny; Joung, J. Keith; Liu, Depei; Liu, Dexi; Lochmüller, Hanns; Lustig, Lawrence; Martens, Jeffrey; Massie, Bernard; Mavilio, Fulvio; Mendell, Jerry R.; Nathwani, Amit; Ponder, Katherine; Porteus, Matthew; Puymirat, Jack; Samulski, Jude; Takeda, Shin'Ichi; Thrasher, Adrian; Vandendriessche, Thierry; Wei, Yuquan; Wilson, James M.; Wilton, Steve D.; Wolfe, John H.; Gao, Guangping.

In: Molecular Therapy, Vol. 21, No. 2, 01.02.2013, p. 266-268.

Research output: Contribution to journalLetter

Tremblay, JP, Xiao, X, Aartsma-Rus, A, Barbas, C, Blau, HM, Bogdanove, AJ, Boycott, K, Braun, S, Breakefield, XO, Bueren, JA, Buschmann, M, Byrne, BJ, Calos, M, Cathomen, T, Chamberlain, J, Chuah, M, Cornetta, K, Davies, KE, Dickson, JG, Duchateau, P, Flotte, TR, Gaudet, D, Gersbach, CA, Gilbert, R, Glorioso, J, Herzog, RW, High, KA, Huang, W, Huard, J, Joung, JK, Liu, D, Liu, D, Lochmüller, H, Lustig, L, Martens, J, Massie, B, Mavilio, F, Mendell, JR, Nathwani, A, Ponder, K, Porteus, M, Puymirat, J, Samulski, J, Takeda, SI, Thrasher, A, Vandendriessche, T, Wei, Y, Wilson, JM, Wilton, SD, Wolfe, JH & Gao, G 2013, 'Translating the genomics revolution: The need for an international gene therapy consortium for monogenic diseases', Molecular Therapy, vol. 21, no. 2, pp. 266-268. https://doi.org/10.1038/mt.2013.4
Tremblay, Jacques P. ; Xiao, Xiao ; Aartsma-Rus, Annemieke ; Barbas, Carlos ; Blau, Helen M. ; Bogdanove, Adam J. ; Boycott, Kym ; Braun, Serge ; Breakefield, Xandra O. ; Bueren, Juan A. ; Buschmann, Michael ; Byrne, Barry J. ; Calos, Michele ; Cathomen, Toni ; Chamberlain, Jeffrey ; Chuah, Marinee ; Cornetta, Kenneth ; Davies, Kay E. ; Dickson, J. George ; Duchateau, Philippe ; Flotte, Terence R. ; Gaudet, Daniel ; Gersbach, Charles A. ; Gilbert, Renald ; Glorioso, Joseph ; Herzog, Roland W. ; High, Katherine A. ; Huang, Wenlin ; Huard, Johnny ; Joung, J. Keith ; Liu, Depei ; Liu, Dexi ; Lochmüller, Hanns ; Lustig, Lawrence ; Martens, Jeffrey ; Massie, Bernard ; Mavilio, Fulvio ; Mendell, Jerry R. ; Nathwani, Amit ; Ponder, Katherine ; Porteus, Matthew ; Puymirat, Jack ; Samulski, Jude ; Takeda, Shin'Ichi ; Thrasher, Adrian ; Vandendriessche, Thierry ; Wei, Yuquan ; Wilson, James M. ; Wilton, Steve D. ; Wolfe, John H. ; Gao, Guangping. / Translating the genomics revolution : The need for an international gene therapy consortium for monogenic diseases. In: Molecular Therapy. 2013 ; Vol. 21, No. 2. pp. 266-268.
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